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Collaborative data collection by TREAT-NMD Registries to support post-marketing surveillance in Spinal Muscular Atrophy

Publication Type: Scientific poster, presentation or proceeding Authors: Miriam Rodrigues; JoAnne Bullivant; Victoria Hodgkinson; TREAT-NMD Registry Curators; Marlène Jagut; Volker Straub; Nathalie ...

Comparative Profiling of Ubiquitin Proteasome System Interplay with Influenza A Virus PB2 Polymerase Protein Recapitulating Virus Evolution in Humans

Publication Type: Peer reviewed scientific article Authors: Elise Biquand; Juline Poirson; Karim, Marwah; Marion Declercq; Nicolas Malausse; Patricia Cassonnet; Cyril Barbezange; Marie-Laure Straub ...

The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations

Joncourt,F.; Diaz-Manera,J.; Gallardo,E.; A.A. Karaduman; Topaloglu,H.; R. El Sherif; Stringer,A.; Shatillo,A.V.; A.S. Martin; H.L. Peay; Bellgard,M.I.; Kirschner,J.; Flanigan,K.M.; Straub,V.; Bushby,K.; ...

The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia

Publication Type: Peer reviewed scientific article Authors: Bladen,C.L.; Rafferty,K.; Straub,V.; Monges,S.; Moresco,A.; Dawkins,H.; A. Roy; Chamova,T.; Guergueltcheva,V.; Korngut,L.; Campbell,C.; ...

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