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Collaborative data collection by TREAT-NMD Registries to support post-marketing surveillance in Spinal Muscular Atrophy

Publication Type: Scientific poster, presentation or proceeding Authors: Miriam Rodrigues; JoAnne Bullivant; Victoria Hodgkinson; TREAT-NMD Registry Curators; Marlène Jagut; Volker Straub; Nathalie ...

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