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Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease.
Christopher; Lindvall, Bjorn; Luebbe, Elizabeth; Lusakowska, Anna; Mazanec, Radim; Meola, Giovanni; Liannna, Orlando; Takahashi, Masanori; Stojan, Peric; Puymirat, Jack; Vidosava, Rakocevic-Stojanovic; ...