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Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease.

Bjorn Lindvall; Elizabeth Luebbe; Anna Lusakowska; Radim Mazanec; Giovanni Meola; Lianna Orlando; Masanori P Takahashi; Stojan Peric; Jack Puymirat; Rakocevic-Stojanovic, Vidosava; Miriam Rodrigues; ...

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