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The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations
Mutation Neuromuscular disease Neuromuscular Diseases observed organization Planning Point Mutation Research Research Support SB- IM Sites STORAGE Therapy Type UK Universities university Abstract: Analyzing ...
The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia
Institute IS journal Medicine Muscular Dystrophies Muscular dystrophy national Network Neuromuscular disease Neuromuscular Diseases ON organization outcome outcomes Patient Patient registry patients ...