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Nusinersen treatment significantly improves hand grip strength, hand motor function and MRC sum scores in adult patients with spinal muscular atrophy types 3 and 4

Publication Type: Peer reviewed scientific article Authors: Bram De Wel; Veerle Goosens; Atka Sobota; Elke Van Camp; Ellen Geukens; Griet Van Kerschaver; Marlène Jagut; Kathleen Claes; Kristl G. ...

Belgian NMD registry

Publication Type: Scientific poster, presentation or proceeding Authors: Marjan Cosyns; Marlène Jagut Source: TGDOC Annual Curators meeting, TREAT-NMD, teleconference (2020) Keywords: Belgian ...

Collaborative data collection by TREAT-NMD Registries to support post-marketing surveillance in Spinal Muscular Atrophy

Publication Type: Scientific poster, presentation or proceeding Authors: Miriam Rodrigues; JoAnne Bullivant; Victoria Hodgkinson; TREAT-NMD Registry Curators; Marlène Jagut; Volker Straub; Nathalie ...

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