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Clinical Evolution and Disease Burden of Cystic Fibrosis Patients after Newborn Screening and Clinical Diagnosis

Publication Type: Dissertation Authors: Noelia Rodriguez Mier; Simeon Wanyama; Géraldine Daneau; Proesmans, Marijke Source: KU Leuven, Leuven, Belgium (2020) Keywords: Cystic Fibrosis mucoviscidose Neonatal Screening Health Topics:  Cystic fibrosis Cystis ...

The burden of cystic fibrosis in Belgium: a registry-based study

Disability-Adjusted Life Years Mucoviscidosis Abstract: Background: Cystic fibrosis is the most common life-limiting autosomal recessive disease among people of European heritage. This rare disease is known to cause ...

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