Résultats de la recherche - 2 results
The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations
Mutation Neuromuscular disease Neuromuscular Diseases observed organization Planning Point Mutation Research Research Support SB- IM Sites STORAGE Therapy Type UK Universities university Abstract: Analyzing ...
The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia
patient outcomes. TREAT- NMD is a worldwide network for neuromuscular diseases that provides an infrastructure to support the delivery of promising new therapies for patients. The harmonized implementation ...