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The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations

Databases Development Diagnostics disease Diseases Duchenne muscular dystrophy electronic Frequency Genetic Genetic Therapy global im Institute IS journal Medicine Muscular Dystrophies Muscular dystrophy ...

The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia

Institute IS journal Medicine Muscular Dystrophies Muscular dystrophy national Network Neuromuscular disease Neuromuscular Diseases ON organization outcome outcomes Patient Patient registry patients ...

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