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Rapport annuel- registre belge des maladies neuromusculaires 2015

tends to decrease year after year. 152 deaths occurred in 2015. Amongst them, 96 occurred in patients suffering from amyotrophic lateral sclerosis. For the year 2015, the ten most prevalent diseases in ...

Early stages of building a rare disease registry, methods and 2010 data from the Belgian Neuromuscular Disease Registry (BNMDR).

Belg, Volume 115, Issue 2, p.97-104 (2015) Keywords: Adult Belgium cross-sectional studies Female Humans Male middle aged Neuromuscular Diseases Online Systems prevalence Rare diseases REGISTRIES ...

The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia

POPULATION prevalence protein Rare disease REGISTRIES Registry successful Therapy UK utilization Abstract: Duchenne muscular dystrophy (DMD) is an X-linked genetic disease, caused by the absence of the ...

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