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The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations

Chan,S.; Korngut,L.; Campbell,C.; Dai,Y.; Wang,J.; Barisic,N.; Brabec,P.; Lahdetie,J.; Walter,M.C.; O. Schreiber-Katz; Karcagi,V.; Garami,M.; Viswanathan,V.; Bayat,F.; Buccella,F.; Kimura,E.; Koeks,Z.; van ...

The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia

Bayat,F.; I. De La Caridad Sarmiento; Ambrosini,A.; Ceradini,F.; Kimura,E.; van den Bergen,J.C.; Rodrigues,M.; Roxburgh,R.; Lusakowska,A.; Oliveira,J.; Santos,R.; Neagu,E.; Butoianu,N.; Artemieva,S.; ...

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