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The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia

Bayat,F.; I. De La Caridad Sarmiento; Ambrosini,A.; Ceradini,F.; Kimura,E.; van den Bergen,J.C.; Rodrigues,M.; Roxburgh,R.; Lusakowska,A.; Oliveira,J.; Santos,R.; Neagu,E.; Butoianu,N.; Artemieva,S.; ...

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