Zoekresultaten - 7 results

Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease.

TREAT- NMD (a global alliance with the mission of improving trial readiness for neuromuscular diseases) and the Marigold Foundation held a workshop of key opinion leaders to agree a minimal dataset for ...

How robust is ACTIVLIM for the follow-up of activity limitations in patients with neuromuscular diseases?

Disorders, Volume 26, Issue 3 (2016) Keywords: Activity limitations Neuromuscular Diseases Patient-reported outcome measure Rasch analysis Abstract: This study aims to investigate the clinimetric properties of ...

Early stages of building a rare disease registry, methods and 2010 data from the Belgian Neuromuscular Disease Registry (BNMDR).

Belg, Volume 115, Issue 2, p.97-104 (2015) Keywords: Adult Belgium cross-sectional studies Female Humans Male middle aged Neuromuscular Diseases Online Systems prevalence Rare diseases REGISTRIES ...

The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations

Mutation Neuromuscular disease Neuromuscular Diseases observed organization Planning Point Mutation Research Research Support SB- IM Sites STORAGE Therapy Type UK Universities university Abstract: Analyzing ...

The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia

Institute IS journal Medicine Muscular Dystrophies Muscular dystrophy national Network Neuromuscular disease Neuromuscular Diseases ON organization outcome outcomes Patient Patient registry patients ...

First epidemiological study on exposure to Neospora caninum in different canine populations in the Algiers District (Algeria)14

0 a Agreement Algeria an Animals antibodies Antibodies,Protozoan Antibody Area article AS aspects Belgium blood Breeding Cattle cause Coccidiosis data differences disease Disease Transmission,Infectious Diseases ...

Evaluation of a SRS2 sandwich commercial enzyme-linked immunosorbent assay for the detection of anti-Neospora caninum antibodies in bovine and canine sera20

EVALUATION Faculty im immunology IS journal Kappa Laboratories Medicine methods Monoclonal antibodies monoclonal-antibodies n Neospora Neuromuscular disease ON parasitology POPULATION Populations prevalence ...

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