Zoekresultaten - 2 results

An EU task force to assess the burden of rare diseases

Publication Type: Peer reviewed scientific article Authors: Pavel Kolkhir; Diana Alecsandra Grad; Periklis Charalampous; Claudia Cruz Oliveira; Enkeleint A Mechili; Brigid Unim; David A Pearce; Marcus Maurer; Brecht Devleesschauwer; Juanita Haagsma Source ...

The health and economic burden of haemophilia in Belgium: a rare, expensive and challenging disease

healthy life years lost due to living with disability and dying prematurely. An incidence perspective was used in line with World Health Organization recommendations. The economic burden calculated from ...

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