A retrospective, non-interventional cohort study to compare adults with SMA receiving risdiplamwith untreated patients: Study design. [1]
Scientific poster, presentation or proceeding
Anglais
SCIENSANO
Auteurs
A Simpson [3]; M. Batech [4]; A. Carmona [5]; S. Lee [6]; A. Poll [7]; S. Edwards [8]; C. Guittari [9]; C. Sutherland [10]; C. Marini-Bettolo [11]; M. Walter [12]; Marlène Jagut [13]; J. Haberlová [14]; V. Hodgkinson [15]; E. Yiu [16]; L. Murphy [17]; TREAT-NMD Global Data systems Oversight Committee (TGDOC) [18]; TREAT-NMD Global Registry Network for SMA [19]; T. Roe [20]; H. Gordish-Dressman [21]Mots-clés
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