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How robust is ACTIVLIM for the follow-up of activity limitations in patients with neuromuscular diseases?
https://doi-org.vdicp.health.fgov.be/10.1016/j.nmd.2015.12.004 Full text language: English Category: A1 ...
Early stages of building a rare disease registry, methods and 2010 data from the Belgian Neuromuscular Disease Registry (BNMDR).
Belg, Volume 115, Issue 2, p.97-104 (2015) Keywords: Adult Belgium cross-sectional studies Female Humans Male middle aged Neuromuscular Diseases Online Systems prevalence Rare diseases REGISTRIES ...
The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations
Verschuuren,J.; Aartsma-Rus,A.; Beroud,C.; Lochmuller,H. Source: Hum.Mutat., Volume 36, Issue 4, Number 402, p.395- 402 (2015) Keywords: a ALL an analysi analysis article Benefit care Clinical data Database ...