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Treatment burden in patients with at least one class IV or V CFTR mutation

Publication Type: Peer reviewed scientific article Authors: Dewulf, Jonas; Vermeulen, François; Simeon Wanyama; Muriel Thomas; Proesmans, Marijke; Dupont, Lieven; De Boeck, Kris Source: Pediatr ...

Is there evidence for correct diagnosis in cystic fibrosis registries?

Publication Type: Peer reviewed scientific article Authors: Muriel Thomas; Lemonnier, Lydie; Gulmans, Vincent; Naehrlich, Lutz; Vermeulen, François; Cuppens, Harry; Castellani, Carlo; Norek, ...

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