Search results - 3 results
A retrospective, non-interventional cohort study to compare adults with SMA receiving risdiplamwith untreated patients: Study design.
Walter, M.; Marlène Jagut; Haberlová, J.; Hodgkinson, V.; Yiu, E.; Murphy, L.; TREAT-NMD Global Data systems Oversight Committee (TGDOC); TREAT-NMD Global Registry Network for SMA; Roe, T.; ...
International collaboration to improve knowledge on myotonic dystrophy type 2
myotonic dystrophy type 2 non-invasive ventilation pacemaker Registry Abstract: Background: The TREAT- NMD Global Registry Network is a global collaboration of neuromuscular disease registries, including ...
Belgian neuromuscular diseases registry (BNMDR): Annual report 2017
/Becker Muscular Dystrophy (BMD) and SMA, the registry also collects additional data within the international TREAT- NMD network (Translational Research in Europe – Assessment and Treatment of NeuroMuscular ...