Résultats de la recherche - 2 results
An EU task force to assess the burden of rare diseases
Marcus Maurer; Brecht Devleesschauwer; Juanita Haagsma Source: Nat Med, Volume 29, Issue 3, Number 517 (2023) Keywords: Advisory Committees European Union Humans Rare diseases Health Topics: Burden of ...
The health and economic burden of haemophilia in Belgium: a rare, expensive and challenging disease
Orphanet J Rare Dis, Volume 9 (2014) Keywords: Belgium Blood Coagulation Factors Cohort Studies Cost of Illness Hemophilia A Humans Abstract: BACKGROUND: Haemophilia is a rare hereditary haemorrhagic disease ...