- Bedoelde u
- perspective studies
Zoekresultaten - 2 results
A retrospective, non-interventional cohort study to compare adults with SMA receiving risdiplamwith untreated patients: Study design.
Publication Type: Scientific poster, presentation or proceeding Authors: Simpson, A.; Batech, M.; Carmona, A.; Lee, S.; Poll, A.; Edwards, S.; Guittari, C.; Sutherland, C.; Marini-Bettolo, C.; Walter, M.; Marlène Jagut; Haberlová, J.; Hodgkinson, V.; Yiu, ...
Early stages of building a rare disease registry, methods and 2010 data from the Belgian Neuromuscular Disease Registry (BNMDR).
Retrospective Studies Abstract: The Belgian Neuromuscular Disease Registry, commissioned in 2008, aims to collect data to improve knowledge on neuromuscular diseases and enhance quality health services for ...